Unraveling the Misconception: The Quest for a “Porphyric Hemophilia Cure” and the Hope of Gene Therapy
Introduction Imagine a world where the simplest bruise spirals into a life-threatening bleed, or where unexplained abdominal pain and neurological disturbances become a constant, debilitating presence. Now, imagine these two worlds colliding, leading to a tangled web of confusion and a desperate search for a cure. This is often the reality for those navigating the…
